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    • Home-Based Care for Patients with Lysosomal Storage Disease: Experiences in Argentina 

      Brunelli, Maria.; Rabhansl, Maria.; Delacre, Clara.; Dankert, Maria.; Cuevillas, Maria.; Frias, Catalina (Latin American Society Inborn Errors and Neonatal Screening, 2019-07-01)
      ABSTRACT Enzyme replacement therapy (ERT) is a long term treatment for patients who suffer from lysosomal storage disease. A transversal descriptive study was conducted to evaluate advantages and disadvantages of a ...